Description and Brand Names

Drug information provided by: Merative, Micromedex®

US Brand Name

  1. Lenmeldy

Descriptions


Atidarsagene autotemcel injection is used to treat children with pre-symptomatic late infantile (PSLI), pre-symptomatic early juvenile (PSEJ), or early symptomatic early juvenile (ESEJ) metachromatic leukodystrophy (MLD).

Metachromatic leukodystrophy (MLD) is a rare genetic disorder that affects the brain and nervous system caused by a deficiency of an enzyme called arylsulfatase A (ARSA).

This medicine is to be given only by or under the immediate supervision of your doctor.

This product is available in the following dosage forms:

  • Suspension